Orphan Diseases Market Size, Type Analysis, Application Analysis, End-Use, Industry Analysis, Regional Outlook, Competitive Strategies And Forecasts, 2023-2032

  • Report ID: ME_0062415
  • Format: Electronic (PDF)
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  • Number of Pages: 250
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Market Snapshot

CAGR:9.46
2023
2032

Source: Market Expertz

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Study Period 2019-2032
Base Year 2023
Forcast Year 2023-2032
CAGR 9.46
Healthcare-companies
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Report Overview

Summary

An orphan disease is defined as a condition that affects fewer than 200,000 people nationwide. This includes diseases as familiar as cystic fibrosis, Lou Gehrig's disease, and Tourette's syndrome, and as unfamiliar as Hamburger disease, Job syndrome, and acromegaly, or "gigantism." Some diseases have patient populations of fewer than a hundred.
New rare diseases are discovered every year. Most are inherited and caused by alterations or defects in genes (mutations). Others can be acquired as a result of environmental and toxic conditions. Genes are pieces of DNA, part of the code that determines the traits and individual characteristics of all living things.
In 2019, the global Orphan Diseases market size was xx million US$ and it is expected to reach xx million US$ by the end of 2026, with a CAGR of xx% between 2019 and 2026.

This report studies the Orphan Diseases market size by players, regions, product types and end industries, history data 2014-2019 and forecast data 2019-2026; This report also studies the global market competition landscape, market drivers and trends, opportunities and challenges, risks and entry barriers, sales channels, distributors and Porter's Five Forces Analysis.

This report focuses on the global top players, covered
Bristol-Myers Squibb
Novartis
Celgene
Roche
Pfizer
Alexion
Sanofi
Vertex Pharmaceuticals
GlaxoSmithKline
Merck
Abbvie

Market segment by Regions/Countries, this report covers
North America
Europe
China
Rest of Asia Pacific
Central & South America
Middle East & Africa

Market segment by Type, the product can be split into
Autoimmune Disorders
Genetic Disorders
Blood Disorders
Cancer
Growth Disorder
Cardiovascular Diseases
Neurological Disorders
Respiratory Disorders
Digestive Disorders
Eye Disorders

Market segment by Application, the market can be split into
Hospitals And Clinics
Research Laboratories

The study objectives of this report are:
To study and forecast the market size of Orphan Diseases in global market.
To analyze the global key players, SWOT analysis, value and global market share for top players.
To define, describe and forecast the market by type, end use and region.
To analyze and compare the market status and forecast among global major regions.
To analyze the global key regions market potential and advantage, opportunity and challenge, restraints and risks.
To identify significant trends and factors driving or inhibiting the market growth.
To analyze the opportunities in the market for stakeholders by identifying the high growth segments.
To strategically analyze each submarket with respect to individual growth trend and their contribution to the market
To analyze competitive developments such as expansions, agreements, new product launches, and acquisitions in the market.
To strategically profile the key players and comprehensively analyze their growth strategies.

In this study, the years considered to estimate the market size of Orphan Diseases are as follows:
History Year: 2014-2019
Base Year: 2019
Estimated Year: 2019
Forecast Year 2019 to 2026
For the data information by region, company, type and application, 2019 is considered as the base year. Whenever data information was unavailable for the base year, the prior year has been considered.

Key Stakeholders
Raw material suppliers
Distributors/traders/wholesalers/suppliers
Regulatory bodies, including government agencies and NGO
Commercial research & development (R&D) institutions
Importers and exporters
Government organizations, research organizations, and consulting firms
Trade associations and industry bodies
End-use industries

Available Customizations
With the given market data, QYResearch offers customizations according to the company's specific needs. The following customization options are available for the report:
Further breakdown of Orphan Diseases market on basis of the key contributing countries.
Detailed analysis and profiling of additional market players.
Table of Contents

Orphan Diseases Market Report by Company, Regions, Types and Applications, Global Status and Forecast to 2025
1 Industry Overview of Orphan Diseases
1.1 Orphan Diseases Market Overview
1.1.1 Orphan Diseases Product Scope
1.1.2 Market Status and Outlook
1.2 Global Orphan Diseases Market Size and Analysis by Regions
1.2.1 North America
1.2.2 Europe
1.2.3 China
1.2.4 Rest of Asia Pacific
1.2.5 Central & South America
1.2.6 Middle East & Africa
1.3 Orphan Diseases Market by Type
1.3.1 Autoimmune Disorders
1.3.2 Genetic Disorders
1.3.3 Blood Disorders
1.3.4 Cancer
1.3.5 Growth Disorder
1.3.6 Cardiovascular Diseases
1.3.7 Neurological Disorders
1.3.8 Respiratory Disorders
1.3.9 Digestive Disorders
1.3.10 Eye Disorders
1.4 Orphan Diseases Market by End Users/Application
1.4.1 Hospitals And Clinics
1.4.2 Research Laboratories

2 Global Orphan Diseases Competition Analysis by Players
2.1 Orphan Diseases Market Size (Value) by Players (2018 and 2019)
2.2 Competitive Status and Trend
2.2.1 Market Concentration Rate
2.2.2 Product/Service Differences
2.2.3 New Entrants
2.2.4 The Technology Trends in Future

3 Company (Top Players) Profiles
3.1 Bristol-Myers Squibb
3.1.1 Company Profile
3.1.2 Main Business/Business Overview
3.1.3 Products, Services and Solutions
3.1.4 Orphan Diseases Revenue (Value) (2014-2019)
3.1.5 Recent Developments
3.2 Novartis
3.2.1 Company Profile
3.2.2 Main Business/Business Overview
3.2.3 Products, Services and Solutions
3.2.4 Orphan Diseases Revenue (Value) (2014-2019)
3.2.5 Recent Developments
3.3 Celgene
3.3.1 Company Profile
3.3.2 Main Business/Business Overview
3.3.3 Products, Services and Solutions
3.3.4 Orphan Diseases Revenue (Value) (2014-2019)
3.3.5 Recent Developments
3.4 Roche
3.4.1 Company Profile
3.4.2 Main Business/Business Overview
3.4.3 Products, Services and Solutions
3.4.4 Orphan Diseases Revenue (Value) (2014-2019)
3.4.5 Recent Developments
3.5 Pfizer
3.5.1 Company Profile
3.5.2 Main Business/Business Overview
3.5.3 Products, Services and Solutions
3.5.4 Orphan Diseases Revenue (Value) (2014-2019)
3.5.5 Recent Developments
3.6 Alexion
3.6.1 Company Profile
3.6.2 Main Business/Business Overview
3.6.3 Products, Services and Solutions
3.6.4 Orphan Diseases Revenue (Value) (2014-2019)
3.6.5 Recent Developments
3.7 Sanofi
3.7.1 Company Profile
3.7.2 Main Business/Business Overview
3.7.3 Products, Services and Solutions
3.7.4 Orphan Diseases Revenue (Value) (2014-2019)
3.7.5 Recent Developments
3.8 Vertex Pharmaceuticals
3.8.1 Company Profile
3.8.2 Main Business/Business Overview
3.8.3 Products, Services and Solutions
3.8.4 Orphan Diseases Revenue (Value) (2014-2019)
3.8.5 Recent Developments
3.9 GlaxoSmithKline
3.9.1 Company Profile
3.9.2 Main Business/Business Overview
3.9.3 Products, Services and Solutions
3.9.4 Orphan Diseases Revenue (Value) (2014-2019)
3.9.5 Recent Developments
3.10 Merck
3.10.1 Company Profile
3.10.2 Main Business/Business Overview
3.10.3 Products, Services and Solutions
3.10.4 Orphan Diseases Revenue (Value) (2014-2019)
3.10.5 Recent Developments
3.11 Abbvie

4 Global Orphan Diseases Market Size by Type and Application (2014-2019)
4.1 Global Orphan Diseases Market Size by Type (2014-2019)
4.2 Global Orphan Diseases Market Size by Application (2014-2019)
4.3 Potential Application of Orphan Diseases in Future
4.4 Top Consumer/End Users of Orphan Diseases

5 North America Orphan Diseases Development Status and Outlook
5.1 North America Orphan Diseases Market Size (2014-2019)
5.2 North America Orphan Diseases Market Size and Market Share by Players (2018 and 2019)

6 Europe Orphan Diseases Development Status and Outlook
6.1 Europe Orphan Diseases Market Size (2014-2019)
6.2 Europe Orphan Diseases Market Size and Market Share by Players (2018 and 2019)

7 China Orphan Diseases Development Status and Outlook
7.1 China Orphan Diseases Market Size (2014-2019)
7.2 China Orphan Diseases Market Size and Market Share by Players (2018 and 2019)

8 Rest of Asia Pacific Orphan Diseases Development Status and Outlook
8.1 Rest of Asia Pacific Orphan Diseases Market Size (2014-2019)
8.2 Rest of Asia Pacific Orphan Diseases Market Size and Market Share by Players (2018 and 2019)

9 Central & South America Orphan Diseases Development Status and Outlook
9.1 Central & South America Orphan Diseases Market Size (2014-2019)
9.2 Central & South America Orphan Diseases Market Size and Market Share by Players (2018 and 2019)

10 Middle East & Africa Orphan Diseases Development Status and Outlook
10.1 Middle East & Africa Orphan Diseases Market Size (2014-2019)
10.2 Middle East & Africa Orphan Diseases Market Size and Market Share by Players (2018 and 2019)

11 Market Forecast by Regions, Type and Application (2019-2025)
11.1 Global Orphan Diseases Market Size (Value) by Regions (2019-2025)
11.1.1 North America Orphan Diseases Revenue and Growth Rate (2019-2025)
11.1.2 Europe Orphan Diseases Revenue and Growth Rate (2019-2025)
11.1.3 China Orphan Diseases Revenue and Growth Rate (2019-2025)
11.1.4 Rest of Asia Pacific Orphan Diseases Revenue and Growth Rate (2019-2025)
11.1.5 Central & South America Orphan Diseases Revenue and Growth Rate (2019-2025)
11.1.6 Middle East & Africa Orphan Diseases Revenue and Growth Rate (2019-2025)
11.2 Global Orphan Diseases Market Size (Value) by Type (2019-2025)
11.3 Global Orphan Diseases Market Size by Application (2019-2025)

12 Orphan Diseases Market Dynamics
12.1 Orphan Diseases Market Opportunities
12.2 Orphan Diseases Challenge and Risk
12.2.1 Competition from Opponents
12.2.2 Downside Risks of Economy
12.3 Orphan Diseases Market Constraints and Threat
12.3.1 Threat from Substitute
12.3.2 Government Policy
12.3.3 Technology Risks
12.4 Orphan Diseases Market Driving Force
12.4.1 Growing Demand from Emerging Markets
12.4.2 Potential Application

13 Market Effect Factors Analysis
13.1 Technology Progress/Risk
13.1.1 Substitutes
13.1.2 Technology Progress in Related Industry
13.2 Consumer Needs Trend/Customer Preference
13.3 External Environmental Change
13.3.1 Economic Fluctuations
13.3.2 Other Risk Factors

14 Research Finding/Conclusion

15 Appendix
Methodology
Analyst Introduction
Data Source


List of Tables and Figures

Figure Orphan Diseases Product Scope
Figure Global Orphan Diseases Market Size (Million USD) (2014-2019)
Table Global Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Figure Global Orphan Diseases Market Share by Regions in 2018
Figure North America Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Figure Europe Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Figure China Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Figure Rest of Asia Pacific Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Figure Central & South America Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Figure Middle East & Africa Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Figure Global Orphan Diseases Market Share by Type in 2018
Figure Autoimmune Disorders Market Size (Million USD) and Growth Rate (2014-2019)
Figure Genetic Disorders Market Size (Million USD) and Growth Rate (2014-2019)
Figure Blood Disorders Market Size (Million USD) and Growth Rate (2014-2019)
Figure Cancer Market Size (Million USD) and Growth Rate (2014-2019)
Figure Growth Disorder Market Size (Million USD) and Growth Rate (2014-2019)
Figure Cardiovascular Diseases Market Size (Million USD) and Growth Rate (2014-2019)
Figure Neurological Disorders Market Size (Million USD) and Growth Rate (2014-2019)
Figure Respiratory Disorders Market Size (Million USD) and Growth Rate (2014-2019)
Figure Digestive Disorders Market Size (Million USD) and Growth Rate (2014-2019)
Figure Eye Disorders Market Size (Million USD) and Growth Rate (2014-2019)
Figure Global Orphan Diseases Market Share by Application in 2018
Table Key Downstream Customer in Hospitals And Clinics
Figure Orphan Diseases Market Size (Million USD) and Growth Rate in Hospitals And Clinics (2014-2019)
Table Key Downstream Customer in Research Laboratories
Figure Orphan Diseases Market Size (Million USD) and Growth Rate in Research Laboratories (2014-2019)
Table Orphan Diseases Market Size (Million USD) by Players (2018 and 2019)
Figure Orphan Diseases Market Size Share by Players in 2018
Figure Orphan Diseases Market Size Share by Players in 2019
Table Bristol-Myers Squibb Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Bristol-Myers Squibb (2014-2019)
Figure Bristol-Myers Squibb Orphan Diseases Business Revenue Market Share in 2018
Table Novartis Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Novartis (2014-2019)
Figure Novartis Orphan Diseases Business Revenue Market Share in 2018
Table Celgene Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Celgene (2014-2019)
Figure Celgene Orphan Diseases Business Revenue Market Share in 2018
Table Roche Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Roche (2014-2019)
Figure Roche Orphan Diseases Business Revenue Market Share in 2018
Table Pfizer Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Pfizer (2014-2019)
Figure Pfizer Orphan Diseases Business Revenue Market Share in 2018
Table Alexion Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Alexion (2014-2019)
Figure Alexion Orphan Diseases Business Revenue Market Share in 2018
Table Sanofi Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Sanofi (2014-2019)
Figure Sanofi Orphan Diseases Business Revenue Market Share in 2018
Table Vertex Pharmaceuticals Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Vertex Pharmaceuticals (2014-2019)
Figure Vertex Pharmaceuticals Orphan Diseases Business Revenue Market Share in 2018
Table GlaxoSmithKline Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of GlaxoSmithKline (2014-2019)
Figure GlaxoSmithKline Orphan Diseases Business Revenue Market Share in 20187
Table Merck Basic Information List
Table Orphan Diseases Business Revenue (Million USD) of Merck (2014-2019)
Figure Merck Orphan Diseases Business Revenue Market Share in 2018
Table Abbvie Basic Information List
Table Global Orphan Diseases Market Size (Million USD) by Type (2014-2019)
Figure Global Orphan Diseases Market Size Share by Type in 2014
Figure Global Orphan Diseases Market Size Share by Type in 2015
Figure Global Orphan Diseases Market Size Share by Type in 2016
Figure Global Orphan Diseases Market Size Share by Type in 2017
Figure Global Orphan Diseases Market Size Share by Type in 2018
Figure Global Orphan Diseases Market Size Share by Type in 2019
Table Global Orphan Diseases Market Size (Million USD) by Application (2014-2019)
Figure Global Orphan Diseases Market Size (Million USD) by Application in 2014
Figure Global Orphan Diseases Market Size (Million USD) by Application in 2015
Figure Global Orphan Diseases Market Size (Million USD) by Application in 2015
Figure Global Orphan Diseases Market Size (Million USD) by Application in 2017
Figure Global Orphan Diseases Market Size (Million USD) by Application in 2018
Figure Global Orphan Diseases Market Size (Million USD) by Application in 2019
Table Top Consumer/End Users of Orphan Diseases
Figure North America Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Table North America Orphan Diseases Market Size (Million USD) by Players (2014-2019)
Figure North America Orphan Diseases Market Size Share by Players in 2018
Figure North America Orphan Diseases Market Size Share by Players in 2019
Figure Europe Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Table Europe Orphan Diseases Market Size (Million USD) by Players (2014-2019)
Figure Europe Orphan Diseases Market Size Share by Players in 2018
Figure Europe Orphan Diseases Market Size Share by Players in 2019
Figure China Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Table China Orphan Diseases Market Size (Million USD) by Players (2014-2019)
Figure China Orphan Diseases Market Size Share by Players in 2018
Figure China Orphan Diseases Market Size Share by Players in 2019
Figure Rest of Asia Pacific Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Table Rest of Asia Pacific Orphan Diseases Market Size (Million USD) by Players (2014-2019)
Figure Rest of Asia Pacific Orphan Diseases Market Size Share by Players in 2018
Figure Rest of Asia Pacific Orphan Diseases Market Size Share by Players in 2019
Figure Central & South America Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Table Central & South America Orphan Diseases Market Size (Million USD) by Players (2014-2019)
Figure Central & South America Orphan Diseases Market Size Share by Players in 2018
Figure Central & South America Orphan Diseases Market Size Share by Players in 2019
Figure Middle East & Africa Orphan Diseases Market Size (Million USD) and Growth Rate by Regions (2014-2019)
Table Middle East & Africa Orphan Diseases Market Size (Million USD) by Players (2014-2019)
Figure Middle East & Africa Orphan Diseases Market Size Share by Players in 2018
Figure Middle East & Africa Orphan Diseases Market Size Share by Players in 2019
Figure Global Orphan Diseases Market Size (Million USD) by Regions (2019-2025)
Table Global Orphan Diseases Market Size (Million USD) by Regions (2019-2025)
Figure Global Orphan Diseases Market Size Share by Regions in 2019
Figure Global Orphan Diseases Market Size Share by Regions in 2025
Figure North America Orphan Diseases Revenue (Million USD) and Growth Rate (2019-2025)
Figure Europe Orphan Diseases Revenue (Million USD) and Growth Rate (2019-2025)
Figure China Orphan Diseases Revenue (Million USD) and Growth Rate (2019-2025)
Figure Rest of Asia Pacific Orphan Diseases Revenue (Million USD) and Growth Rate (2019-2025)
Figure Central & South America Orphan Diseases Revenue (Million USD) and Growth Rate (2019-2025)
Figure Middle East & Africa Orphan Diseases Revenue (Million USD) and Growth Rate (2019-2025)
Table Global Orphan Diseases Market Size (Million USD) by Type (2019-2025)
Figure Global Orphan Diseases Market Size Share by Type in 2019
Figure Global Orphan Diseases Market Size Share by Type in 2025
Table Global Orphan Diseases Market Size (Million USD) by Application (2019-2025)
Figure Global Orphan Diseases Market Size (Million USD) by Application in 2019
Figure Global Orphan Diseases Market Size (Million USD) by Application in 2025

RESEARCH METHODOLOGY

A research methodology is a systematic approach for assessing or conducting a market study. Researchers tend to draw on a variety of both qualitative and quantitative study methods, inclusive of investigations, survey, secondary data and market observation.

Such plans can focus on classifying the products offered by leading market players or simply use statistical models to interpret observations or test hypotheses. While some methods aim for a detailed description of the factors behind an observation, others present the context of the current market scenario.

Now letā€™s take a closer look at the research methods here.

Secondary Research Model

Extensive data is obtained and cumulated on a substantial basis during the inception phase of the research process. The data accumulated is consistently filtered through validation from the in-house database, paid sources as well reputable industry magazines. A robust research study requires an understanding of the overall value chain. Annual reports and financials of industry players are studied thoroughly to have a comprehensive idea of the market taxonomy.

Primary Insights

Post conglomeration of the data obtained through secondary research; a validation process is initiated to verify the numbers or figures. This process is usually performed by having a detailed discussion with the industry experts.

However, we do not restrict our primary interviews only to the industry leaders. Our team covers the entire value chain while verifying the data. A significant number of raw material suppliers, local manufacturers, distributors, and stakeholders are interviewed to make our findings authentic. The current trends which include the drivers, restraints, and opportunities are also derived through the primary research process.

Market Estimation

The market estimation is conducted by analyzing the data collected through both secondary and primary research. This process involves market breakdown, bottom-up and top- down approach.

Moreover, while forecasting the market a comprehensive statistical time series model is designed for each market. Macroeconomic indicators are considered to understand the current trends of the market. Each data point is verified by the process of data triangulation method to arrive at the final market estimates.

Final Presentation

The penultimate process results in a holistic research report. The study equips key industry players to undertake significant strategic decisions through the findings. The report encompasses detailed market information. Graphical representations of the current market trends are also made available in order to make the study highly comprehensible for the reader.

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